The combination of gene therapy and stem cell therapy has shown long-term success in treating rare skin disease
Scientists reported the long-term success of an experimental operation in 2015 to transplant skin from genetically modified stem cells to a child with epidermolysis bullosa (EB). For the first time, a team of therapists from Germany and Italy could save a patient whose skin surface had been destroyed by 80%. However, doctors were unsure if the treatment would be successful in the long term and if the skin would remain stable.